Buckle up, it's going to be an incredible ride, columnist Helen Baldwin says in a letter to her 13-year-old self.

Many SMA patients continue to see gains in motor function with long-term Spinraza treatment, a real-world study from ...

Meeting your new medical team is never easy, especially when you have a complex and rare disease like SMA, columnist Alyssa ...

The use of salbutamol may improve upper limb strength and aid breathing in young children with spinal muscular atrophy, an analysis found.